Di(heptadecan-9-yl) 8,8'-((3-(dimethylamino)propyl)azanediyl)dioctanoate
Registry Number 2985009-50-3
100 mg/$5,000
For Research Use Only.
Sold under the Hatch-Waxman exemption (safe harbor exemption)
Di(heptadecan-9-yl) 8,8'-((3-(dimethylamino)propyl)azanediyl)dioctanoate
Registry Number 2985009-50-3
100 mg/$5,000
For Research Use Only.
Sold under the Hatch-Waxman exemption (safe harbor exemption)
Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease
Authors: Kiran Musunuru, M.D., Ph.D. et al.
Published May 15, 2025
DOI: 10.1056/NEJMoa2504747
